Search All Tech Briefings


Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available.  Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

| 79 Results

Title
Intervention Indication Therapeutic Area Year Actions
Brolucizumab for visual impairment due to diabetic macular oedema Brolucizumab (RTH258; ESBA1008; Beovu) Visual impairment Endocrine Nutritional and Metabolic Disorders , Ophthalmology 2020 View  |  Download
Burosumab for x-linked hypophosphataemia in adults Burosumab (Crystiva; KRN23) Hypophosphataemia Endocrine Nutritional and Metabolic Disorders 2020 View  |  Download
CAEL-101 for treating amyloid light chain amyloidosis CAEL-101 Amyloid light chain amyloidosis Endocrine Nutritional and Metabolic Disorders 2022 View  |  Download
Canagliflozin for chronic kidney disease in adult patients with type 2 diabetes mellitus Canagliflozin (Invokana; canagliflozin hemihydrate) Diabetic nephropathy Endocrine Nutritional and Metabolic Disorders , Nephrology 2019 View  |  Download
Canagliflozin for type 2 diabetes mellitus in children and adolescents Canagliflozin (Invokana; canagliflozin hemihydrate) Type 2 diabetes Endocrine Nutritional and Metabolic Disorders 2023 View  |  Download
CER-001 for Familial Primary Hypoalphalipoproteinemia CER-001 Familial primary hypoalphalipoproteinemia Endocrine Nutritional and Metabolic Disorders , Genetic Disorders 2018 View  |  Download
Cipaglucosidase alfa/miglustat for treating children and adolescents with late-onset Pompe disease Cipaglucosidase alfa/miglustat (AT-GAA;;Zavesca,;OGT 918;BBDF101) Pompe disease Endocrine Nutritional and Metabolic Disorders , Genetic Disorders 2023 View  |  Download
Daratumumab in addition to cyclophosphamide, bortezomib and dexamethasone for newly diagnosed systemic amyloid light-chain amyloidosis Bortezomib (Velcade; bortezomib mannitol boronic ester) , Cyclophosphamide (Procytox; cyclophosphamide monohydrate) , Daratumumab (Darzalex; JNJ-54767414) , Dexamethasone (dexamethasone sodium metasulfobenzoate) Amyloidosis Endocrine Nutritional and Metabolic Disorders 2020 View  |  Download
Dasiglucagon for treating congenital hyperinsulinism Dasiglucagon (ZP 4207) Congenital hyperinsulinism , Hypoglycaemia Endocrine Nutritional and Metabolic Disorders 2021 View  |  Download
Deferiprone for transfusional iron overload in sickle cell disease and other anaemias – First Line Deferiprone (Ferriprox) Iron overload Endocrine Nutritional and Metabolic Disorders , Haematology 2020 View  |  Download
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