Search All Tech Briefings

Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available. Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

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Title	Intervention	Indication	Therapeutic Area	Year	Actions
Emicizumab for mild or moderate haemophilia A	Emicizumab (Hemlibra)	Haemophilia A	Haematology	2021	View \| Download
Etranacogene dezaparvovec for treating moderately severe or severe haemophilia B	Etranacogene Dezaparvovec (AMT-061; AAV5-hFIXco-Padua)	Haemophilia B	Haematology	2020	View \| Download
Fedratinib for Myelofibrosis	Fedratinib (SAR302503)	Myelofibrosis	Haematological Cancer and Lymphomas , Haematology	2018	View \| Download
Fidanacogene elaparvovec for haemophilia B	Fidanacogene elaparvovec (SPK-9001)	Haemophilia B	Haematology	2021	View \| Download
Giroctocogene fitelparvovec for haemophilia A	Giroctocogene fitelparvovec	Haemophilia A	Haematology	2023	View \| Download
Givosiran for acute hepatic porphyria (AHP)	Givosiran (ALN-AS1)	Acute hepatic porphyria (AHP)	Haematology , Hepatology	2018	View \| Download
Iptacopan for paroxysmal nocturnal haemoglobinuria	Iptacopan	Paroxysmal nocturnal haemoglobinuria (PNH)	Haematology	2022	View \| Download
L-glutamine for Sickle Cell Disease	L-glutamine (Xyndari)	Sickle cell disease (SCD)	Haematology	2018	View \| Download
Luspatercept for adult patients with beta-thalassemia who require red blood cell transfusions	Luspatercept (ACE-536; Reblozyl)	Beta thalassemia	Genetic Disorders , Haematology	2018	View \| Download
Luspatercept for myelodysplastic syndromes (MDS) associated anaemia	Luspatercept (ACE-536; Reblozyl)	Anaemia due to myelodysplastic syndromes (MDS)	Haematological Cancer and Lymphomas , Haematology	2018	View \| Download