Search All Tech Briefings

Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available. Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

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Title	Intervention	Indication	Therapeutic Area	Year	Actions
Luspatercept for the treatment of adults with non-transfusion dependent beta-thalassaemia	Luspatercept (ACE-536; Reblozyl)	Beta thalassemia	Genetic Disorders , Haematology	2020	View \| Download
Marstacimab for the treatment of haemophilia A and haemophilia B	Marstacimab (PF-06741086)	Haemophilia A , Haemophilia B	Haematology	2023	View \| Download
Mim8 for prophylaxis of haemophilia A	NNC0365-3769	Haemophilia A	Haematology	2023	View \| Download
Momelotinib for the treatment of symptomatic and anaemic myelofibrosis	Momelotinib	Anaemic myelofibrosis	Haematological Cancer and Lymphomas , Haematology	2022	View \| Download
Pegcetacoplan (APL-2) for paroxysmal nocturnal haemoglobinuria	Pegcetacoplan (APL-2)	Paroxysmal nocturnal haemoglobinuria (PNH)	Haematology	2019	View \| Download
Ravulizumab (subcutaneous formulation) for treating paroxysmal nocturnal haemoglobinuria and atypical haemolytic uraemic syndrome	Ravulizumab (ALXN1210; Ultomiris)	Atypical haemolytic uraemic syndrome (aHUS) , Paroxysmal nocturnal haemoglobinuria (PNH)	Haematology , Nephrology	2022	View \| Download
Ravulizumab for atypical haemolytic uraemic syndrome in adults and children – first line	Ravulizumab (ALXN1210; Ultomiris)	Atypical haemolytic uraemic syndrome (aHUS)	Haematology , Nephrology	2018	View \| Download
Ravulizumab for paroxysmal nocturnal haemoglobinuria in paediatrics	Ravulizumab (ALXN1210; Ultomiris)	Paroxysmal nocturnal haemoglobinuria (PNH)	Haematology	2021	View \| Download
Ravulizumab for treating thrombotic microangiopathies following haematopoietic stem cell transplantation in children	Ravulizumab (ALXN1210; Ultomiris)	Thrombotic microangiopathies	Haematology	2023	View \| Download
Rezafungin for previously untreated invasive candidiasis	Rezafungin (CD101)	Invasive candidasis	Haematology , Infectious Disease	2022	View \| Download