Search All Tech Briefings


Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available.  Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

| 2 Results

Title
Intervention Indication Therapeutic Area Year Actions
Migalastat for Fabry disease in children aged 12 to 15 years Migalastat hydrochloride (Galafold; AT1001) Fabry disease Endocrine Nutritional and Metabolic Disorders , Genetic Disorders 2019 View  |  Download
Pegunigalsidase alfa for Fabry disease – first-line PRX-102 (Pegunigalsidase alfa) Fabry disease Endocrine Nutritional and Metabolic Disorders , Genetic Disorders 2020 View  |  Download
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