Voxelotor is as an oral, once-daily therapy that is being developed for treatment of SCD. It is designed to work by helping haemoglobin hold onto more oxygen as the red blood cells travel through the body. This keeps red blood cells in their normal shape and helps stop sickling. As there is a desperate need for new treatments for SCD, voxelotor, if licensed, will offer a new treatment option for patients with SCD.
Voxelotor for Sickle Cell Disease
Interventions: Voxelotor (GBT-440)
Indications: Sickle cell anaemia
Therapeutic Areas: Haematology