Search All Tech Briefings


Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available.  Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

| 5 Results

Title
Intervention Indication Therapeutic Area Year Actions
Domagrozumab (PF-6252616) for Duchenne muscular dystrophy in children and adolescents Domagrozumab (PF-06252616) Duchenne muscular dystrophy (DMD) Genetic Disorders , Musculoskeletal System 2017 View  |  Download
Edasalonexent for Duchene muscular dystrophy Edasalonexent (CAT-1004) Duchenne muscular dystrophy (DMD) Genetic Disorders , Musculoskeletal System 2020 View  |  Download
Fordadistrogene movaparvovec for Duchenne muscular dystrophy Fordadistrogene movaparvovec Duchenne muscular dystrophy (DMD) Genetic Disorders , Musculoskeletal System 2022 View  |  Download
rAAVrh74.MHCK7.micro-dystrophin for Duchenne muscular dystrophy Microdystrophin (SRP-9001; rAAVrh74.MHCK7) Duchenne muscular dystrophy (DMD) Genetic Disorders , Musculoskeletal System 2020 View  |  Download
Vamorolone for treating Duchenne muscular dystrophy Vamorolone (VBP15) Duchenne muscular dystrophy (DMD) Genetic Disorders , Musculoskeletal System 2021 View  |  Download
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