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Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available.  Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

| 8 Results

Title
Intervention Indication Therapeutic Area Year Actions
ABP 959 for treating paroxysmal nocturnal
haemoglobinuria
ABP 959 Paroxysmal nocturnal haemoglobinuria (PNH) Haematology 2022 View  |  Download
ALXN 1210 for Paroxysmal Nocturnal Haemoglobinuria – First Line Ravulizumab (ALXN1210; Ultomiris) Paroxysmal nocturnal haemoglobinuria (PNH) Haematology 2017 View  |  Download
Crovalimab for treatment of paroxysmal nocturnal haemoglobinuria Crovalimab Paroxysmal nocturnal haemoglobinuria (PNH) Haematology 2022 View  |  Download
Danicopan with eculizumab or ravulizumab for treating paroxysmal nocturnal haemoglobinuria Danicopan (ACH-0144471; ACH-4471; ALXN2040) , Ravulizumab (ALXN1210; Ultomiris) Paroxysmal nocturnal haemoglobinuria (PNH) Haematology 2022 View  |  Download
Iptacopan for paroxysmal nocturnal haemoglobinuria Iptacopan Paroxysmal nocturnal haemoglobinuria (PNH) Haematology 2022 View  |  Download
Pegcetacoplan (APL-2) for paroxysmal nocturnal haemoglobinuria Pegcetacoplan (APL-2) Paroxysmal nocturnal haemoglobinuria (PNH) Haematology 2019 View  |  Download
Ravulizumab (subcutaneous formulation) for treating paroxysmal nocturnal haemoglobinuria and atypical haemolytic uraemic syndrome Ravulizumab (ALXN1210; Ultomiris) Atypical haemolytic uraemic syndrome (aHUS) , Paroxysmal nocturnal haemoglobinuria (PNH) Haematology , Nephrology 2022 View  |  Download
Ravulizumab for paroxysmal nocturnal haemoglobinuria in paediatrics Ravulizumab (ALXN1210; Ultomiris) Paroxysmal nocturnal haemoglobinuria (PNH) Haematology 2021 View  |  Download
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