Search All Tech Briefings


Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available.  Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

| 3 Results

Title
Intervention Indication Therapeutic Area Year Actions
ATB200/AT2221 for Late onset Pompe disease in adults and adolescents over 12 years – first line ATB200/AT2221 Pompe disease Endocrine Nutritional and Metabolic Disorders , Genetic Disorders 2020 View  |  Download
Avalglucosidase alfa for late-onset Pompe disease Avalglucosidase alfa (neoGAA; GZ-402666) Pompe disease Endocrine Nutritional and Metabolic Disorders , Genetic Disorders 2019 View  |  Download
Cipaglucosidase alfa/miglustat for treating children and adolescents with late-onset Pompe disease Cipaglucosidase alfa/miglustat (AT-GAA;;Zavesca,;OGT 918;BBDF101) Pompe disease Endocrine Nutritional and Metabolic Disorders , Genetic Disorders 2023 View  |  Download
Medicines
Medicine Industry's Gateway to NICE
Support for Industry
Outputs & Publications