Somapacitan is in clinical development for the treatment of small for gestational age or Noonan syndrome or idiopathic short stature in patients aged 2 to 18 years. Idiopathic short stature is defined as shortness in childhood without a specific cause. This condition may be familial (run in families) or nonfamilial and may be associated with […]
Govorestat is in clinical development for treating classic galactosemia. Classic galactosemia is a rare disorder affecting the body’s ability to break down (metabolise) the sugar present in milk (galactose) into another type of sugar called glucose. Glucose provides a source of energy for body cells. Classic galactosemia is caused by a faulty (mutated) gene, meaning […]
Camlipixant is in clinical development for the treatment of adults with refractory or unexplained chronic cough. Cough is a normal reflex response to airway irritation, triggered by stimulation of airway cough receptors, which protect against choking and enhance airway clearance. Chronic cough is a persistent cough that lasts for eight weeks or longer. Refractory cough […]
Baloxavir marboxil is in clinical development for reducing direct transmission of influenza.Influenza commonly known as flu is an infection of the nose, throat, and lungs, which are a partof the respiratory system. There are three types of viruses that cause influenza; type A, B and C.Type A and B influenza viruses cause the main outbreaks […]
Bemarituzumab in combination with chemotherapy is in clinical development for the treatment of previously untreated locally advanced, or metastatic gastric or gastroesophageal junction (GEJ) cancer. Gastric (or stomach) cancer is when abnormal cells in the stomach start to grow and divide in an uncontrolled way. GEJ cancer starts in the junction where the food pipe […]
Vimseltinib is in development to treat tenosynovial giant cell tumour (TGCT) in adults. TGCTs are rare but non-cancerous tumours that develop in tissues around joints. TGCTs can be diffuse, meaning the tumour affects most of a large joint (e.g., knee), or localised, meaning the tumour is limited to a specific area of the joint (normally […]
Iclepertin is in clinical development for treating cognitive (thinking) impairment associated with schizophrenia (CIAS). Schizophrenia is a long-term mental health condition, which can be triggered by many different biological, social and psychological factors. The symptoms of schizophrenia are usually divided into positive symptoms (such as hallucinations and delusions), negative symptoms (such as emotional apathy, lack […]
Imetelstat is in clinical development for the treatment of intermediate-2 or high-risk myelofibrosis (MF) in patients who are relapsed (the disease has come back) or refractory (the disease has stopped responding to a treatment) to Janus-Kinase (JAK) inhibitor treatment. MF is a rare blood cancer that causes scarring of the bone marrow which makes it […]
Sumatriptan-naproxen is for the acute treatment of migraine. Migraine is a headache that is usually characterised by throbbing in one side of the head and other symptoms including sensitivity to light and sound, nausea and vomiting. The cause of migraines is not known but triggers include tiredness, anxiety and caffeine. Migraines are also thought to […]
Epcoritamab is in clinical development for the treatment of adult patients with relapsed or refractory diffuse large B-cell lymphoma (DLBCL) after one or more lines of therapy. DLBCL is a cancer of B cells, a type of immune cell, and the most common type of fast-growing non-Hodgkin’s lymphoma - a disease in which cancer cells […]
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