Search All Tech Briefings

Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available.  Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

| 51 Results

Intervention Indication Therapeutic Area Year Actions
Emicizumab for mild or moderate haemophilia A Emicizumab (Hemlibra) Haemophilia A Haematology 2021 View  |  Download
Etranacogene dezaparvovec for treating moderately severe or severe haemophilia B Etranacogene Dezaparvovec (AMT-061; AAV5-hFIXco-Padua) Haemophilia B Haematology 2020 View  |  Download
Fedratinib for Myelofibrosis Fedratinib (SAR302503) Myelofibrosis Haematological Cancer and Lymphomas , Haematology 2018 View  |  Download
Fidanacogene elaparvovec for haemophilia B Fidanacogene elaparvovec (SPK-9001) Haemophilia B Haematology 2021 View  |  Download
Giroctocogene fitelparvovec for haemophilia A Giroctocogene fitelparvovec Haemophilia A Haematology 2023 View  |  Download
Givosiran for acute hepatic porphyria (AHP) Givosiran (ALN-AS1) Acute hepatic porphyria (AHP) Haematology , Hepatology 2018 View  |  Download
Imetelstat for treating relapsed or refractory intermediate-2 or high-risk myelofibrosis after janus kinase inhibitor treatment Imlunestrant Myelofibrosis Haematological Cancer and Lymphomas , Haematology 2024 View  |  Download
Iptacopan for paroxysmal nocturnal haemoglobinuria Iptacopan Paroxysmal nocturnal haemoglobinuria (PNH) Haematology 2022 View  |  Download
L-glutamine for Sickle Cell Disease L-glutamine (Xyndari) Sickle cell disease (SCD) Haematology 2018 View  |  Download
Luspatercept for adult patients with beta-thalassemia who require red blood cell transfusions Luspatercept (ACE-536; Reblozyl) Beta thalassemia Genetic Disorders , Haematology 2018 View  |  Download
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