Search All Tech Briefings

Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available. Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

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Title	Intervention	Indication	Therapeutic Area	Year	Actions
Crovalimab for treatment of paroxysmal nocturnal haemoglobinuria	Crovalimab	Paroxysmal nocturnal haemoglobinuria (PNH)	Haematology	2022	View \| Download
CTX001 for severe sickle cell disease	CTX001	Leukocyte adhesion deficiency , Sickle cell disease (SCD)	Haematology , Immunology	2021	View \| Download
CTX001 for transfusion-dependent beta-thalassaemia	CTX001	Beta thalassemia	Genetic Disorders , Haematology	2021	View \| Download
Danicopan with eculizumab or ravulizumab for treating paroxysmal nocturnal haemoglobinuria	Danicopan (ACH-0144471; ACH-4471; ALXN2040) , Ravulizumab (ALXN1210; Ultomiris)	Paroxysmal nocturnal haemoglobinuria (PNH)	Haematology	2022	View \| Download
Daprodustat for anaemia associated with chronic kidney disease	Daprodustat (GSK1278863)	Anaemia	Cardiovascular System , Haematology , Nephrology	2021	View \| Download
Darbepoetin alfa (Aranesp) for treatment of anaemia in adults with low or intermediate-1-risk myelodysplastic syndromes	Darbepoetin alfa (Aranesp)	Anaemia	Haematology	2017	View \| Download
Deferiprone for transfusional iron overload in sickle cell disease and other anaemias – First Line	Deferiprone (Ferriprox)	Iron overload	Endocrine Nutritional and Metabolic Disorders , Haematology	2020	View \| Download
Dersimelagon for previously untreated erythropoietic protoporphyria and X-linked protoporphyria	Dersimelagon	Erythropoietic protoporphyria , X-linked protoporphyria	Dermatology , Haematology	2022	View \| Download
Efanesoctocog alfa for treating and preventing bleeding in people with haemophilia A who have been previously treated	Efanesoctocog alfa	Haemophilia A	Haematology	2022	View \| Download
Efgartigimod PH20 SC for adults with primary immune thrombocytopenia	Efgartigimod PH20 SC	Immune thrombocytopenia (ITP)	Haematology , Immunology	2023	View \| Download