Search All Tech Briefings


Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available.  Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

| 52 Results

Title
Intervention Indication Therapeutic Area Year Actions
Crizanlizumab for the prevention of recurrent vaso-occlusive crises in children with sickle cell disease Crizanlizumab (SEG101; Adakveo) Sickle cell disease (SCD) Haematology 2022 View  |  Download
Crovalimab for treatment of paroxysmal nocturnal haemoglobinuria Crovalimab Paroxysmal nocturnal haemoglobinuria (PNH) Haematology 2022 View  |  Download
CTX001 for severe sickle cell disease CTX001 Leukocyte adhesion deficiency , Sickle cell disease (SCD) Haematology , Immunology 2021 View  |  Download
CTX001 for transfusion-dependent beta-thalassaemia CTX001 Beta thalassemia Genetic Disorders , Haematology 2021 View  |  Download
Danicopan with eculizumab or ravulizumab for treating paroxysmal nocturnal haemoglobinuria Danicopan (ACH-0144471; ACH-4471; ALXN2040) , Ravulizumab (ALXN1210; Ultomiris) Paroxysmal nocturnal haemoglobinuria (PNH) Haematology 2022 View  |  Download
Daprodustat for anaemia associated with chronic kidney disease Daprodustat (GSK1278863) Anaemia Cardiovascular System , Haematology , Nephrology 2021 View  |  Download
Darbepoetin alfa (Aranesp) for treatment of anaemia in adults with low or intermediate-1-risk myelodysplastic syndromes Darbepoetin alfa (Aranesp) Anaemia Haematology 2017 View  |  Download
Deferiprone for transfusional iron overload in sickle cell disease and other anaemias – First Line Deferiprone (Ferriprox) Iron overload Endocrine Nutritional and Metabolic Disorders , Haematology 2020 View  |  Download
Dersimelagon for previously untreated erythropoietic protoporphyria and X-linked protoporphyria Dersimelagon Erythropoietic protoporphyria , X-linked protoporphyria Dermatology , Haematology 2022 View  |  Download
Efanesoctocog alfa for treating and preventing bleeding in people with haemophilia A who have been previously treated Efanesoctocog alfa Haemophilia A Haematology 2022 View  |  Download
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